Gene therapy

June 30, 2015

Gene therapy was the subject covered in the best video produced by students in the 2014-15 cohort of Medical Biochemists at the University of Leicester.

This is an excellent example of “whiteboard animation” – you don’t get such an effective result without significant planning. The video is wrong to say treatment of X-SCID was the first successful use; the first case involved Ashanti DeSilva, who had ADA-SCID. It does not include any coverage of genome editing methods, which are the most exciting new development in this area. Nevertheless, a very useful primer on the topic.